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NT14025

Role of rare variants in genetic predisposition to statin myopathy

Project goals

The project objective is to determine the contribution of rare gene variants in SLCO1B1, SLCO1B3, and other known or unknown candidate genes to the mechanism of statin-induced myopathy. The presence of variants in approximately 70 patients with statin myopathy will be determined combination of genomic methods. The results will be validated by standard techniques of mutation analysis and evaluated using bioinformatics tools.

Keywords

statinmyopathySLCO1B1SLCO1B3

Public support

  • Provider

    Ministry of Health

  • Programme

    Ministry of Health?s Departmental Research and Development Programme III

  • Call for proposals

    VaV pro Ministerstvo zdravotnictví III 4 (SMZ0201301)

  • Main participants

  • Contest type

    VS - Public tender

  • Contract ID

    NT14025-3/2013

Alternative language

  • Project name in Czech

    Úloha vzácných variant v genetické predispozici ke statiny indukované myopatii

  • Annotation in Czech

    Cílem projektu je zjistit příspěvek vzácných genových variant v SLCO1B1, SLCO1B3 a v dalších známých či dosud neznámých kandidátních genech k mechanismu vzniku statiny indukované myopatie. Přítomnost variant u cca 70 nemocných se statinovou myopatií bude zjišťována kombinací genomických metod. Výsledky budou validovány standardními technikami mutační analýzy a zhodnoceny pomocí bioinformatických nástrojů.

Scientific branches

  • R&D category

    NV - Nonindustrial research (Applied research excluded Industrial research)

  • CEP classification - main branch

    FA - Cardiovascular diseases including cardio-surgery

  • CEP - secondary branch

  • CEP - another secondary branch

  • 30201 - Cardiac and Cardiovascular systems

Completed project evaluation

  • Provider evaluation

    V - Vynikající výsledky projektu (s mezinárodním významem atd.)

  • Project results evaluation

    The authors demonstrated significance of certain loci to be genotypized in case of Statins praescriptions.

Solution timeline

  • Realization period - beginning

    May 1, 2013

  • Realization period - end

    Dec 31, 2015

  • Project status

    U - Finished project

  • Latest support payment

    Mar 20, 2015

Data delivery to CEP

  • Confidentiality

    S - Úplné a pravdivé údaje o projektu nepodléhají ochraně podle zvláštních právních předpisů

  • Data delivery code

    CEP16-MZ0-NT-U/02:1

  • Data delivery date

    Dec 19, 2016

Finance

  • Total approved costs

    5,865 thou. CZK

  • Public financial support

    5,865 thou. CZK

  • Other public sources

    0 thou. CZK

  • Non public and foreign sources

    0 thou. CZK

Basic information

Recognised costs

5 865 CZK thou.

Public support

5 865 CZK thou.

100%


Provider

Ministry of Health

CEP

FA - Cardiovascular diseases including cardio-surgery

Solution period

01. 05. 2013 - 31. 12. 2015