Gene therapy of monogenic diseases
The result's identifiers
Result code in IS VaVaI
<a href="https://www.isvavai.cz/riv?ss=detail&h=RIV%2F67985904%3A_____%2F20%3A00536561" target="_blank" >RIV/67985904:_____/20:00536561 - isvavai.cz</a>
Result on the web
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DOI - Digital Object Identifier
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Alternative languages
Result language
angličtina
Original language name
Gene therapy of monogenic diseases
Original language description
Gene therapy repairs or modifies the expression of individual gene in targeted cells by transfer of nucleic material to the cells. The development of the gene therapy has been impressive over the last decade. It can reduce the production of mutated proteins causing the disease, elevate the production of proteins curing the disease, or produce modified or new proteins. Here we briefly review the main alternatives of gene targeting together with the options of delivery to the cells.
Czech name
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Czech description
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Classification
Type
C - Chapter in a specialist book
CEP classification
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OECD FORD branch
10603 - Genetics and heredity (medical genetics to be 3)
Result continuities
Project
<a href="/en/project/LO1609" target="_blank" >LO1609: Models of the Serious Human Diseases: Traumatic Spinal Cord Injury, Huntington’s Disease, Melanoma and Infertility</a><br>
Continuities
I - Institucionalni podpora na dlouhodoby koncepcni rozvoj vyzkumne organizace
Others
Publication year
2020
Confidentiality
S - Úplné a pravdivé údaje o projektu nepodléhají ochraně podle zvláštních právních předpisů
Data specific for result type
Book/collection name
Translational Research in Serious Human Diseases
ISBN
978-80-200-3158-7
Number of pages of the result
6
Pages from-to
148-153
Number of pages of the book
271
Publisher name
Academia
Place of publication
Praha
UT code for WoS chapter
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