European regulation on orphan medicinal products: 10 years of experience and future perspectives
The result's identifiers
Result code in IS VaVaI
<a href="https://www.isvavai.cz/riv?ss=detail&h=RIV%2F00064203%3A_____%2F11%3A10293954" target="_blank" >RIV/00064203:_____/11:10293954 - isvavai.cz</a>
Alternative codes found
RIV/00216208:11130/11:10293954
Result on the web
<a href="http://dx.doi.org/10.1038/nrd3445" target="_blank" >http://dx.doi.org/10.1038/nrd3445</a>
DOI - Digital Object Identifier
<a href="http://dx.doi.org/10.1038/nrd3445" target="_blank" >10.1038/nrd3445</a>
Alternative languages
Result language
angličtina
Original language name
European regulation on orphan medicinal products: 10 years of experience and future perspectives
Original language description
In 2000, regulation on orphan medicinal products was adopted in the European Union with the aim of benefiting patients who suffer from serious, rare conditions for which there is currently no satisfactory treatment. Since then, more than 850 orphan drugdesignations have been granted by the European Commission based on a positive opinion from the Committee for Orphan Medicinal Products (COMP), and more than 60 orphan drugs have received marketing authorization in Europe. Here, stimulated by the tenth anniversary of the COMP, we reflect on the outcomes and experience gained in the past decade, and contemplate issues for the future, such as catalysing drug development for the large number of rare diseases that still lack effective treatments.
Czech name
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Czech description
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Classification
Type
J<sub>x</sub> - Unclassified - Peer-reviewed scientific article (Jimp, Jsc and Jost)
CEP classification
FD - Oncology and haematology
OECD FORD branch
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Result continuities
Project
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Continuities
V - Vyzkumna aktivita podporovana z jinych verejnych zdroju
Others
Publication year
2011
Confidentiality
S - Úplné a pravdivé údaje o projektu nepodléhají ochraně podle zvláštních právních předpisů
Data specific for result type
Name of the periodical
Nature Reviews Drug Discovery
ISSN
1474-1776
e-ISSN
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Volume of the periodical
10
Issue of the periodical within the volume
5
Country of publishing house
GB - UNITED KINGDOM
Number of pages
9
Pages from-to
341-349
UT code for WoS article
000290017300016
EID of the result in the Scopus database
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